Orphan Drugs: Why the Designation?
Orphan drugs are medicinal products intended for the diagnosis, prevention, or treatment of life-threatening or very serious diseases or disorders that are rare. A disease or disorder is defined as rare when it affects less than 1 in 2,000 citizens, some rare diseases include Moebius syndrome, Stoneman syndrome, alkaptonuria. These drugs are called “orphans” because, […]









